Out today! Taking the diagnostic challenges from clinic into the lab bench to learn from our rare disease patients
Thanks to David Yule and his team for partnering with us in this project
www.neurology.org/doi/10.1212/...
Background and ObjectivesHeterozygous ITPR1 variants have been previously linked to multiple human disease phenotypes, including
congenital ataxia and Gillespie syndrome. Previous reports have describ...