A baby named KJ, born with a rare genetic disorder called CPS1 deficiency, is thriving thanks to the world’s first personalized gene-editing treatment. 🧬✨
Doctors at @childrensphila.bsky.social used base editing—a tool invented by HHMI Investigator David Liu and his lab at Harvard.
Breaking News: A baby with a rare disorder made medical history by receiving the first custom gene-editing treatment. The technique used has the potential to help people with thousands of other uncommon genetic diseases. nyti.ms/4j49xBy
